The challenge for the first ever in-human gene editing trial, according to today’s guest, is with the delivery to the body. “At the moment, the easiest place to deliver your gene or genome editing is to the liver, using AAV which are viruses that seek out and go to the liver cells," says Sandy Macrae, the CEO of Sangamo Therapeutics. Sangamo is known for two things: They have pioneered the commercialization of an older gene editing technology called Zinc Fingers. And they have done a lot of work in the area of HIV.
The First In-Human Gene Editing Trial in the U.S. - And It’s Not with CRISPR
www.mendelspod.com
The First In-Human Gene Editing Trial in the U.S. - And It’s Not with CRISPR
Mendelspod Podcast
Offering a front row seat to the Century of Biology, veteran podcast host Theral Timpson interviews the who's who in genomics and genomic medicine.
Offering a front row seat to the Century of Biology, veteran podcast host Theral Timpson interviews the who's who in genomics and genomic medicine.Listen on
Substack App
RSS Feed
Appears in episode
Theral Timpson
Recent Episodes
The First In-Human Gene Editing Trial in the U.S. - And It’s Not with CRISPR